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Europe Approves CRISPR Gene-Edited Therapy for Sickle Cell Disease
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The European Commission approves CASGEVY™ (exagamglogene autotemcel) as the first CRISPR/Cas9 gene-edited therapy for severe sickle cell disease and transfusion-dependent beta thalassemia. Vertex leads the development, manufacturing, and commercialization of the therapy under a profit-sharing agreement with CRISPR Therapeutics.
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How does the collaboration between Vertex and CRISPR Therapeutics contribute to the advancement of personalized medicine?
How might the approval of CASGEVY™ impact the treatment landscape for sickle cell disease and beta thalassemia?
What are the potential implications of this gene-edited therapy for other genetic diseases?
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